Monday, February 26, 2018

Scientists move closer to treatment for Huntington's disease

Researchers show that a new version of the CRISPR/Cas9 system -- a modern tool for editing DNA -- is safer and more specific than versions previously used to remove the disease-causing DNA sequence in the defective gene that causes Huntington's disease. The study, which was carried out in cellular models from a Huntington's patient, brings a possible treatment for this currently incurable genetic disease one step closer.
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